Rare: A Rare Disease Revolution

From a soldier to a musician, from an immigrant family to a mother of twins, meet the unsuspecting heroes waging war against rare disease. Love fuels this rare disease revolution, where parents become scientists and warriors, fighting battles in laboratories, in Congress, and in their own homes. Amid an indifferent healthcare system, these families are driving scientific breakthroughs, championing their children’s cause, and advancing hope — and potential cures — for countless others.